A potential new treatment for a rare and devastating bone disorder has been identified by scientists. The disorder, known as Von-Hippel Lindau (VHL) disease, is caused by a genetic mutation that leads to the growth of tumors in various parts of the body. The new treatment, a viral gene therapy, has been found to be effective in a small trial of patients with VHL. The results of the trial, published in Nature, showed that the gene therapy was able to reduce the symptoms of VHL and slow the progression of the disease. The researchers are hopeful that this therapy could offer a much-needed treatment option for those suffering from this devastating disorder.

Read Full Article Here

source: Phys.org